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PPMD Urges UN Support for ‘World Duchenne Awareness Day’ Resolution Ahead of UN General Assembly Meeting

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Solid Biosciences Receives FDA Clearance for Investigational New Drug Application for SGT-003 Gene Therapy Candidate

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Advancing Duchenne Cardiac Care: A Year of Impact and Gratitude

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WATCH: Overview of Topline Results from Phase 3 EMBARK Study (Webinar recording)

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PPMD Provides $250,000 in Funding to Rare Disease Research to Establish New Clinical Trial Site

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WATCH: AGAMREE Approval – What this means for you & your family (Webinar recording)

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Calling All Adults with Duchenne & Becker: Join the 2024 PPMD Adult Advisory Committee (PAAC)

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Defeat Duchenne Canada and PPMD Award $300,000 (USD) Clinical Fellowship in Duchenne Endocrinology and Bone Fragility

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WATCH: Advocating for Access – Overview of Medicaid DUR and P&T Meetings (Webinar Recording)

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Sarepta Therapeutics Announces Topline Results from Phase 3 EMBARK Study of ELEVIDYS Gene Therapy

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