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Blog

Newborn Screening for Duchenne: PPMD’s Collaborative Future Planning Efforts

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Cranbury Pharmaceuticals (Tris Pharma) Receives FDA Approval for First Generic Version of Emflaza® (deflazacort) for Duchenne

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Build Your Own Care Binder at PPMD’s 30th Annual Conference

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Pfizer Shares Update on Phase 3 Study of Investigational Mini-Dystrophin Gene Therapy

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Consensus Statement Featuring Expert Insights from PPMD’s Certified Duchenne Care Centers on Access to Novel Therapies for Duchenne Published

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Roche Announces Phase II Open-Label SHIELD DMD Study to Assess Effect of Satralizumab on Bone Health in Duchenne

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Summer Fun: Accessible Activities for All Ages and Interests

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Capricor Therapeutics Announces Positive 3-Year Efficacy Results from HOPE-2 Open Label Extension Study of CAP-1002

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NS Pharma Shares Update on VILTEPSO® (Viltolarsen) Phase 3 Study

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Dyne Therapeutics Shares New Clinical Data from DELIVER Trial of DYNE-251 in Duchenne Patients

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