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Study to Explore Barriers to Diverse Clinical Trial Participation in Duchenne Published

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PTC Therapeutics Announces European Commission Returns Translarna™ Opinion to CHMP For Re-evaluation

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Congress Passes FAA Reauthorization Featuring Monumental Accessibility Improvements

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Mapping Out a Path Forward: PPMD Convenes Representatives from 21 Academic Centers and 11 Industry Partners for 2024 Cardiac Care Workshop

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PPMD’s Pat Furlong Honored with ASGCT’s Sonia Skarlatos Public Service Award

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Updates from the ACHDNC Meeting and Next Steps for Duchenne Newborn Screening

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PPMD Hosts 2024 Cardiac Workshop, May 9-10

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Update on Pfizer’s Phase 2 Gene Therapy Trial for Duchenne

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WATCH: Community Progress in Duchenne Newborn Screening (Webinar Recording)

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Comprehensive Genetic Counseling Resource for Dystrophinopathies Published: A Collaborative Effort by PPMD and Expert Genetic Counselors

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