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Capricor Therapeutics Plans to File Biologics License Application for Full Approval of Deramiocel for the Treatment of Duchenne Cardiomyopathy

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Wave Life Sciences Announces Positive Interim Data from FORWARD-53 Clinical Trial Evaluating WVE-N531 in Individuals With Duchenne Amenable to Exon 53 Skipping

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Thanks to You PPMD Continues Forward in All Areas of Support

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PPMD Contributes to National Academies Report on Rare Disease Regulatory Processes

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PPMD Community Webinar Recap: Overview of DUVYZAT and Access Resources

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PPMD & Global Patient Advocacy Groups Award BIND Project $113,000 to Further Brain Involvement Research

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Navigating Access & Resources

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Watch the Recording: Advocating for A Successful School Year

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Setting Up A Successful School Year

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Raising Our Voices for Duchenne: Recap of PPMD’s Advocacy Webinar

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