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PTC Therapeutics Provides Regulatory Update on Translarna™ (atalauren)

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Rare Disease Advocacy Delivers: Major Federal Wins for Duchenne and Becker Community

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Cardiac Care for Female Carriers

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PPMD Joins Collaborative Research Effort to Decode How Human Muscle Regenerates

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Sarepta Shares Topline Three-Year EMBARK Data for ELEVIDYS in Ambulatory Duchenne Patients

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Solid Biosciences Shares Update on INSPIRE DUCHENNE Trial Evaluating SGT-003

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PPMD’s Race to End Duchenne Team Member Claims Victories in Both 5K and 10K as Community Raises Funds for Duchenne and Becker Research and Care

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Watch: Capricor Therapeutics — HOPE-3 Community Update (Webinar Recording)

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Historic Victory: Duchenne Added to the Recommended Uniform Screening Panel (RUSP)

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Dyne Therapeutics Announces Positive Topline Results from Phase 1/2 DELIVER Trial of Z-Rostudirsen in Duchenne

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