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Blog

This Year, I Am Grateful For Our Journey Together

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Equitable Access in Clinical Trials—A Call for Action and Collaboration

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WATCH: RGX-202 – AFFINITY DUCHENNE Pivotal Program and Functional Data (Webinar Recording)

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PPMD Culminates 30th Anniversary with Celebratory “Investing in Every Future” Event

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REGENXBIO Initiates Pivotal Phase of AFFINITY DUCHENNE® Trial of RGX-202 Gene Therapy, Reports Positive Functional Data

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REGENXBIO Initiates Pivotal Phase of AFFINITY DUCHENNE® Trial of RGX-202 Gene Therapy, Reports Positive Functional Data

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Calling All Adults with Duchenne & Becker: Join the 2025 PPMD Adult Advisory Committee

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REGENXBIO Shares Updates on Phase I/II AFFINITY DUCHENNE® trial of RGX-202

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Solid Biosciences Shares Updates on INSPIRE DUCHENNE Clinical Trial of SGT-003

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Sarepta Announces Discontinuation of SRP-5051 Development for Duchenne

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