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Edgewise Announces Positive Long-Term Sevasemten Data

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Capricor Therapeutics Announces New PDUFA Date for Deramiocel

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PPMD and FED Announce 2026 Advocacy Leadership Awards Honoring Bipartisan Champions in Congress

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Advocates Unite in Washington to Advance Duchenne and Becker Policy, Mark 25th Anniversary of MD-CARE Act

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PPMD Partners with Cooperative International Neuromuscular Research Group, Global Sponsors to Advance Expanded Duchenne Natural History Study

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25 Years Later: Reflecting on the 2001 MD-CARE Act Hearing and Where We Are Now

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Roche Announces Termination of Phase 2 SHIELD DMD Study

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PTC Therapeutics Provides Regulatory Update on Translarna™ (atalauren)

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Rare Disease Advocacy Delivers: Major Federal Wins for Duchenne and Becker Community

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Cardiac Care for Female Carriers

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