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WATCH: AGAMREE Approval – What this means for you & your family (Webinar recording)

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Calling All Adults with Duchenne & Becker: Join the 2024 PPMD Adult Advisory Committee (PAAC)

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Defeat Duchenne Canada and PPMD Award $300,000 (USD) Clinical Fellowship in Duchenne Endocrinology and Bone Fragility

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WATCH: Advocating for Access – Overview of Medicaid DUR and P&T Meetings (Webinar Recording)

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Sarepta Therapeutics Announces Topline Results from Phase 3 EMBARK Study of ELEVIDYS Gene Therapy

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WATCH: Capricor Therapeutics – CAP-1002 HOPE-3 Program Update (Webinar Recording)

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Edgewise Therapeutics Announces Expansion of their EDG-5506 Clinical Program in Duchenne

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FDA Grants Approval to AGAMREE® (Vamorolone)

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Duchenne Added to New York State’s Newborn Screening Panel

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Community Report: Key Insights from the April 2023 Endocrine and Bone Workshop

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