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REGENXBIO Announces Completion of Enrollment in Cohort 2 and Additional Positive Interim Data in AFFINITY DUCHENNE® Trial

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Duchenne Newborn Screening Bill Passes Arizona Senate

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Watch: Navigating Steroid Choices – Understanding the Process, Pathways, and Policies (Webinar Recording)

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PPMD 2023 Duchenne Early Care Meeting Report Published: Enhancing Support in Early Diagnosis

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Sarepta Therapeutics Reports Positive Data from Part B of MOMENTUM Study of SRP-5051

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Duchenne Added to Minnesota’s Newborn Screening Panel

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CHMP Issues Negative Opinion for Renewal of Conditional Marketing Authorization for Translarna™ (ataluren) in Europe

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Astellas Releases Results of Discontinued Phase 1b Study of ASP0367

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PPMD Hosts 2024 Duchenne Healthcare Professionals Summit

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Introducing PPMD’s Gene Therapy Hub

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