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Italfarmaco Group Announces NDA Accepted for Givinostat

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Edgewise Therapeutics announces positive topline 12-month data from EDG-5506 ARCH study

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FDA grants approval via accelerated approval pathway to ELEVIDYS: First-ever gene therapy for individuals with Duchenne ages 4-5

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Santhera announces exclusive North America license agreement with Catalyst Pharmaceuticals for vamorolone

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Thanks to you PPMD continues forward in all areas of support

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WATCH: ENVISION Study Update With Sarepta Therapeutics (Webinar Recording)

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PPMD Announces Pediatric Certified Duchenne Care Center at Norton Children’s Hospital

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PPMD publishes results of study to understand Duchenne patients’ and caregivers’ perspectives on corticosteroids

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PPMD Announces Pediatric Certified Duchenne Care Center at Boston Children’s Hospital

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PPMD, CureDuchenne, Muscular Dystrophy Association Announce Collaborative Project to Focus on Re-Dosing Gene Therapy in Duchenne Muscular Dystrophy

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