Revised Community-Led Duchenne Guidance Published: Developing Potential Treatments for the Entire Spectrum of Disease ...
PPMD Provides $500,000 in Funding to Kinea Bio Through PPMD Venture Pathways Program to Support Next-Gen Midi-Dystrophin Gene Therapy Development ...
Watch: Dyne Therapeutics — Advancing DYNE-251, an Investigational Medicine for DMD (Webinar Recording) ...
REGENXBIO Announces Completion of Enrollment in Cohort 2 and Additional Positive Interim Data in AFFINITY DUCHENNE® Trial ...
Watch: Navigating Steroid Choices – Understanding the Process, Pathways, and Policies (Webinar Recording) ...