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REGENXBIO Announces RGX-202 Gene Therapy Trial is Active & Recruiting

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PPMD Urges FDA to Conduct a Full Review of Ataluren (Translarna)

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Introducing PPMD Lighthouse Workshops: Let’s Navigate, Together.

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Your Registry Data at Work: More Complete Data Betters Our Understanding of Duchenne & Becker

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Magical Miles & $300,000 Raised with the Race to End Duchenne at Walt Disney World Marathon Weekend

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Update from Santhera & ReveraGen: FDA Acceptance of New Drug Application for Vamorolone in Duchenne

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Thank You for Helping Ensure Hearts Grow Stronger With Every Beat!

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Race Athlete Spotlight: Tammy Cate

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PPMD Submits Written Comments Following CBER Meeting on Patient Perspectives on Gene Therapy Products

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Double Your Gift Today.

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