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Race Athlete Spotlight: Jason Hendry

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Sarepta Announces Biologics License Application (BLA) Accepted For Filing by the FDA for SRP-9001

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This Thanksgiving I am Grateful for You.

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PTC Shares Community Letter Updating on Activities To Bring Ataluren (Translarna) To US Patients

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Pfizer Announces First Participant Dosed in DAYLIGHT Phase 2 Gene Therapy Trial

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PPMD Provides Testimony During FDA CBER Meeting on Patient Perspectives on Gene Therapy Products

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Make PPMD’s commitment to the heart Stronger with Every Beat

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Expert Care in an Emergency: Important Contact Information & Resources

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PPMD Announces Pediatric Certified Duchenne Care Center at Riley Children’s Health

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Astellas Announces Decision to Discontinue Screening & Enrollment Activities for ASP0367 (MA-0211)

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