Skip to main content

Blog

Introducing PPMD’s Newborn Screening Action Center: A Hub for Advocacy and Education

...

Dyne Therapeutics Announces Positive New Clinical Data from Phase 1/2 DELIVER Trial of DYNE-251 in Duchenne

...

Raising Our Voices This Duchenne Action Month

...

Duchenne Added to Massachusetts Newborn Screening Panel

...

WATCH: Advancing DYNE-251 – An Investigational Medicine for Duchenne to Deliver for Patients (Webinar Recording)

...

Finding Support to Manage Behaviors in Duchenne and Becker

...

PPMD Urges FDA to Conduct a Full Review of Ataluren (Translarna) Following Resubmission of NDA

...

WATCH: Edgewise Therapeutics – Clinical Trials in Becker Muscular Dystrophy (Webinar)

...

Avidity Biosciences Announces Positive Data From Phase 1/2 EXPLORE44™ Trial of AOC 1044 in Individuals Amenable to Exon 44 Skipping

...

Your Citizen Science At Work

...