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Expanding Leadership, Accelerating Progress

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Make Your Voice Heard: Support Adding Duchenne to the RUSP

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Solid Biosciences Shares Update on INSPIRE DUCHENNE Trial of SGT-003

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Calling All Adults with Duchenne & Becker: Join the 2026 PPMD Adult Advisory Committee (PAAC)

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Dyne Therapeutics, Inc. announced today FDA Breakthrough Therapy Designation for DYNE-251 in Duchenne Muscular Dystrophy

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Watch: Capricor Therapeutics – Regulatory Update & Clinical Insights on Deramiocel for Duchenne Cardiomyopathy

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Sarepta to Resume ELEVIDYS Shipments to Ambulatory Patients After FDA Recommends Removal of Voluntary Hold for Ambulatory Population

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FDA Grants Breakthrough Therapy Designation to Avidity’s del-zota

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Update on ELEVIDYS Shipments in the U.S.

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ELEVIDYS Update

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