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Finding Belonging and Fostering Community

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Pfizer Discontinues Development of Investigational Mini-Dystrophin Gene Therapy

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Response to the July 29th STAT Article

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Making it Work: Practical Tips for Enhancing Quality of Life

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ITF Therapeutics Announces U.S. Commercial Availability of DUVYZAT™ (givinostat) for Treatment of Duchenne

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Navigating the Approved Therapy Landscape

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PPMD’s 30th Annual Conference Session Recordings

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PPMD Applauds FDA Launch of Rare Disease Innovation Hub — A Milestone for Rare Disease Patients

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Capricor Therapeutics Announces Positive Skeletal Muscle and Cardiac Function Data from HOPE-2 OLE Study Data of Deramiocel (CAP-1002)

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PPMD Convenes Leading Experts to Discuss Topics in Becker Care Ahead of 30th Annual Conference

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