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FibroGen announces discontinuation of LELANTOS-2 Open Label Extension

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Santhera Receives Positive European Medicines Agency (EMA) CHMP Opinion Recommending Approval of Vamorolone in European Union

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Finding and Accepting Help

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What is Palliative Care? Understanding an additional layer of support

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REGENXBIO announces interim clinical data from Phase I/II AFFINITY DUCHENNE™ trial of RGX-202

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WATCH: Advocating for Access: Insurance 101 (Webinar Recording)

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Edgewise Therapeutics Now Enrolling GRAND CANYON Study of EDG-5506 in Individuals with Becker Muscular Dystrophy

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Miles for Matthew Celebrates 15 Years

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CDCC Spotlight: Children’s Hospital Los Angeles

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Entrada Therapeutics starts dosing in ENTR-601-44 Phase 1 trial

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